Muscular Dystrophy, Oculopharyngeal
Showing 1 - 25 of 2,408
Natural History Study of Oculopharyngeal Muscular Dystrophy
Withdrawn
- Oculopharyngeal Muscular Dystrophy
- Non-interventional study
- (no location specified)
May 23, 2022
Muscular Dystrophy, Oculopharyngeal, Ptosis Trial in Caen (Myoblast autologous graft)
Terminated
- Muscular Dystrophy, Oculopharyngeal
- Ptosis
- Myoblast autologous graft
-
Caen, FranceCHU Caen
Nov 23, 2020
Screening in Oculopharyngeal Muscular Dystrophy
Completed
- Oculopharyngeal Muscular Dystrophy
- Videofluoroscopic swallowing study
- +2 more
-
Gainesville, FloridaUniversity of Florida
Mar 25, 2020
Oculopharyngeal Muscular Dystrophy, Muscular Dystrophies, Myopathy; Hereditary Trial in Calgary (Expiratory muscle strength
Not yet recruiting
- Oculopharyngeal Muscular Dystrophy
- +2 more
- Expiratory muscle strength therapy (EMST150, Aspire LLC)
- (no location specified)
Mar 23, 2020
Duchenne Muscular Dystrophy Trial in Cairo (kinesio tape)
Recruiting
- Duchenne Muscular Dystrophy
- kinesio tape
-
Cairo, EgyptNoha Elserty
Jul 22, 2023
Peabody Developmental Motor Scaling In Period Duchenne Muscular
Completed
- Duchenne Muscular Dystrophy (DMD)
- Peabody Developmental Motor Scales-2, PDMS
-
Samsun, TurkeyOndokuz Mayıs University
Aug 6, 2023
Duchenne Muscular Dystrophy Trial (Designed Physical Therapy Program, Bicycle Ergometry Training)
Not yet recruiting
- Duchenne Muscular Dystrophy
- Designed Physical Therapy Program
- Bicycle Ergometry Training
- (no location specified)
May 5, 2023
FSHD, FSHD1, FSHD2 Trial (AOC 1020, Placebo)
Not yet recruiting
- FSHD
- +26 more
- AOC 1020
- Placebo
- (no location specified)
Feb 27, 2023
Becker Muscular Dystrophy Trial in Atlanta (EDG-5506)
Enrolling by invitation
- Becker Muscular Dystrophy
-
Atlanta, GeorgiaRare Disease Research
Sep 27, 2023
Duchenne Muscular Dystrophy, Fascioscapulohumeral Muscular Dystrophy Trial in Liège (ActiMyo)
Recruiting
- Duchenne Muscular Dystrophy
- Fascioscapulohumeral Muscular Dystrophy
- ActiMyo
-
Liège, BelgiumCHR de la Citadelle
Aug 1, 2023
Oculopharyngeal Muscular Dystrophy Trial in Chicoutimi, Montréal, Québec (Trehalose)
Withdrawn
- Oculopharyngeal Muscular Dystrophy
-
Chicoutimi, Quebec, Canada
- +2 more
Jan 10, 2020
Duchenne Muscular Dystrophy Trial in Ankara (Telerehabilitation)
Completed
- Duchenne Muscular Dystrophy
- Telerehabilitation
-
Ankara, TurkeyLokman Hekim University
Oct 26, 2023
FSHD Trial (MSOT Acuity Echo)
Not yet recruiting
- FSHD
- MSOT Acuity Echo
- (no location specified)
Jun 5, 2023
Duchenne Muscular Dystrophy Trial in Chengdu (JWK007 Single intravenous infusion administration)
Recruiting
- Duchenne Muscular Dystrophy
- JWK007 Single intravenous infusion administration
-
Chengdu, Sichuan, ChinaWest China Hospital, Sichuan University
Oct 29, 2023
Duchenne Muscular Dystrophy Video Assessment Registry
Recruiting
- Duchenne Muscular Dystrophy
-
Plymouth, MassachusettsCasimir
Feb 1, 2023
Duchenne Muscular Dystrophy Trial in Ankara (telerehabilitation-based motor imagery training, telerehabilitation-based
Not yet recruiting
- Duchenne Muscular Dystrophy
- telerehabilitation-based motor imagery training
- telerehabilitation-based physiotheraphy training
-
Ankara, TurkeyHacettepe University
Oct 27, 2023
NSAA NON-Interventional Study Protocol
Not yet recruiting
- Duchenne Muscular Dystrophy
- Remote Administration of NSAA
- (no location specified)
Sep 19, 2023
Muscular Dystrophies, Spinal Muscular Atrophy, Duchenne Muscular Dystrophy Trial in Saint Paul (Abilitech Assist)
Recruiting
- Muscular Dystrophies
- +6 more
- Abilitech Assist
-
Saint Paul, MinnesotaGillette Children's
Dec 1, 2022
Duchenne Muscular Dystrophy Trial in Portland (NS-089/NCNP-02)
Not yet recruiting
- Duchenne Muscular Dystrophy
-
Portland, OregonShriners Hospital for Children
Aug 16, 2023
Facio-Scapulo-Humeral Dystrophy Trial (ARO-DUX4 for Injection, Placebo)
Not yet recruiting
- Facio-Scapulo-Humeral Dystrophy
- ARO-DUX4 for Injection
- Placebo
- (no location specified)
Nov 13, 2023
Muscular Dystrophy, Duchenne Type Trial (trunk oriented exercise, whole body vibration)
Not yet recruiting
- Muscular Dystrophy, Duchenne Type
- trunk oriented exercise
- whole body vibration
- (no location specified)
Jan 8, 2023
Facioscapulohumeral Muscular Dystrophy (FSHD) Trial (Placebo, RO7204239)
Recruiting
- Facioscapulohumeral Muscular Dystrophy (FSHD)
- Placebo
- RO7204239
-
København Ø, DenmarkRigshospitalet; Klinik for Nerve- og Muskelsygdomme
Feb 2, 2023
Duchenne Muscular Dystrophy Trial in Los Angeles, Columbus (SGT-003)
Not yet recruiting
- Duchenne Muscular Dystrophy
- SGT-003
-
Los Angeles, California
- +1 more
Nov 14, 2023
Duchenne Muscular Dystrophy Trial (Givinostat, Placebo)
Not yet recruiting
- Duchenne Muscular Dystrophy
- Givinostat
- Placebo
- (no location specified)
Jun 27, 2023